Striated muscle gene therapy for the treatment of lipoprotein lipase deficiency.
Gadek KE, Wang H, Hall MN, Sungello M, Libby A, MacLaskey D, Eckel RH, Olwin BB. Striated muscle gene therapy for the treatment of lipoprotein lipase deficiency. PLoS One. 2018; 13(1):e0190963.